{"id":130,"date":"2026-09-22T13:06:02","date_gmt":"2026-09-22T13:06:02","guid":{"rendered":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/?page_id=130"},"modified":"2026-11-05T18:03:56","modified_gmt":"2026-11-05T18:03:56","slug":"therapeutic-areas","status":"publish","type":"page","link":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/therapeutic-areas\/","title":{"rendered":"Focus Areas"},"content":{"rendered":"<main id='oxy-main'><div class=\"oxy-container-130-205 oxy-container od-page-focus-areas\"><div class=\"oxy-container-130-204 oxy-container od-fx-793346c73\"><section class=\"oxy-container-130-218 oxy-container od-hero\" aria-labelledby=\"focus-title\"><div class=\"oxy-container-130-217 oxy-container od-container\"><div class=\"oxy-container-130-208 oxy-container od-hero-heading\"><div class=\"oxy-svg-icon2-130-206 oxy-svg-icon2 od-hero-icon\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"24\" height=\"24\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><path d=\"M6 18h8\"><\/path><path d=\"M3 22h18\"><\/path><path d=\"M14 22a7 7 0 1 0 0-14h-1\"><\/path><path d=\"M9 14h2\"><\/path><path d=\"M9 12a2 2 0 0 1-2-2V6h6v4a2 2 0 0 1-2 2Z\"><\/path><path d=\"M12 6V3a1 1 0 0 0-1-1H9a1 1 0 0 0-1 1v3\"><\/path><\/svg>\n<\/div><h1 class=\"oxy-text-130-207 oxy-text od-hero-title\" id=\"focus-title\">\nTherapeutic Focus Areas\n<\/h1><\/div><p class=\"oxy-text-130-209 oxy-text od-hero-lead\">\nDedicated expertise in rare disease treatment\n<\/p><p class=\"oxy-text-130-210 oxy-text od-hero-copy\">\nOrphalan focuses on three therapeutic areas in rare diseases: metabolic disorders (including Wilson's disease), West's syndrome and glioblastoma.\n<\/p><div class=\"oxy-container-130-213 oxy-container od-hero-actions\"><a class=\"oxy-text-link-130-211 oxy-text-link od-button od-button--accent od-button--borderless\" href=\"\/products\/\" target=\"_self\">\nView Our Products\n<\/a><a class=\"oxy-text-link-130-212 oxy-text-link od-button od-button--outlined-light\" href=\"\/disease-info\/\" target=\"_self\">\nLearn About Rare Diseases\n<\/a><\/div><button class=\"oxy-container-link-130-216 oxy-container-link od-hero-back od-focus-back\" target=\"_self\" data-interactions=\"[{&quot;trigger&quot;:&quot;click&quot;,&quot;prevent_default&quot;:true,&quot;actions&quot;:[{&quot;name&quot;:&quot;javascript_function&quot;,&quot;js_function_name&quot;:&quot;orphalanHeroBack&quot;}]}]\" id=\"focus-back\" type=\"button\" aria-label=\"Go back to the previous page\"><div class=\"oxy-svg-icon2-130-214 oxy-svg-icon2 od-hero-back-icon\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"24\" height=\"24\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><path d=\"m15 18-6-6 6-6\"><\/path><\/svg>\n<\/div><span class=\"oxy-text-130-215 oxy-text od-link-label\">\nBack\n<\/span><\/button><\/div><\/section><section class=\"oxy-container-130-252 oxy-container od-section\" aria-labelledby=\"focus-expertise-title\"><div class=\"oxy-container-130-251 oxy-container od-container\"><header class=\"oxy-container-130-222 oxy-container od-home-heading\"><span class=\"oxy-text-130-219 oxy-text od-eyebrow\">\nWE SOLVE\n<\/span><h2 class=\"oxy-text-130-220 oxy-text od-home-heading-title od-focus-expertise-title\" id=\"focus-expertise-title\">\nOur Areas of Expertise\n<\/h2><p class=\"oxy-text-130-221 oxy-text od-home-heading-lead od-focus-expertise-lead\">\nWe concentrate our efforts on rare diseases where specialised knowledge and dedicated research can improve patient outcomes and quality of life.\n<\/p><\/header><div class=\"oxy-container-130-250 oxy-container od-focus-area-grid\"><article class=\"oxy-container-130-231 oxy-container od-focus-area-card\"><div class=\"oxy-container-130-224 oxy-container od-focus-area-media\"><img decoding=\"async\" class=\"oxy-image-130-223 oxy-image od-focus-area-image\" src=\"https:\/\/funny-fermi.104-248-174-66.plesk.page\/wp-content\/uploads\/2026\/09\/pexels-C-1843358-scaled.jpg\" alt=\"Patient with Wilson&#039;s disease\" loading=\"lazy\"><\/div><div class=\"oxy-container-130-230 oxy-container od-focus-area-copy\"><h3 class=\"oxy-text-130-225 oxy-text od-card-title\">\nMetabolic Disorders\n<\/h3><p class=\"oxy-text-130-226 oxy-text od-body od-focus-area-description\">\nRare genetic disorders affecting metabolism, including Wilson's disease\n<\/p><a class=\"oxy-container-link-130-229 oxy-container-link od-button od-home-control od-home-control--navy od-focus-area-action\" href=\"\/disease-info\/wilsons-disease\/\" target=\"_self\" aria-label=\"Learn more about Metabolic Disorders\"><span class=\"oxy-text-130-227 oxy-text od-link-label\">\nLearn More\n<\/span><div class=\"oxy-svg-icon2-130-228 oxy-svg-icon2 od-link-icon od-focus-area-arrow\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"24\" height=\"24\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><path d=\"M5 12h14\"><\/path><path d=\"m12 5 7 7-7 7\"><\/path><\/svg>\n<\/div><\/a><\/div><\/article><article class=\"oxy-container-130-240 oxy-container od-focus-area-card\"><div class=\"oxy-container-130-233 oxy-container od-focus-area-media\"><img decoding=\"async\" class=\"oxy-image-130-232 oxy-image od-focus-area-image\" src=\"https:\/\/funny-fermi.104-248-174-66.plesk.page\/wp-content\/uploads\/2026\/09\/Therapeutic_Portfolio_-_Kigabeq-1.jpeg\" alt=\"Child with West&#039;s syndrome receiving care\" loading=\"lazy\"><\/div><div class=\"oxy-container-130-239 oxy-container od-focus-area-copy\"><h3 class=\"oxy-text-130-234 oxy-text od-card-title\">\nWest's Syndrome\n<\/h3><p class=\"oxy-text-130-235 oxy-text od-body od-focus-area-description\">\nA severe form of epilepsy in infancy, also known as infantile spasms\n<\/p><a class=\"oxy-container-link-130-238 oxy-container-link od-button od-home-control od-home-control--navy od-focus-area-action\" href=\"\/disease-info\/wests-syndrome\/\" target=\"_self\" aria-label=\"Learn more about West&#039;s Syndrome\"><span class=\"oxy-text-130-236 oxy-text od-link-label\">\nLearn More\n<\/span><div class=\"oxy-svg-icon2-130-237 oxy-svg-icon2 od-link-icon od-focus-area-arrow\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"24\" height=\"24\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><path d=\"M5 12h14\"><\/path><path d=\"m12 5 7 7-7 7\"><\/path><\/svg>\n<\/div><\/a><\/div><\/article><article class=\"oxy-container-130-249 oxy-container od-focus-area-card\"><div class=\"oxy-container-130-242 oxy-container od-focus-area-media\"><img decoding=\"async\" class=\"oxy-image-130-241 oxy-image od-focus-area-image\" src=\"https:\/\/funny-fermi.104-248-174-66.plesk.page\/wp-content\/uploads\/2026\/09\/young-child-therapy-battling-cancer_de_gauche.jpg\" alt=\"Patient receiving brain tumour treatment\" loading=\"lazy\"><\/div><div class=\"oxy-container-130-248 oxy-container od-focus-area-copy\"><h3 class=\"oxy-text-130-243 oxy-text od-card-title\">\nGlioblastoma\n<\/h3><p class=\"oxy-text-130-244 oxy-text od-body od-focus-area-description\">\nA fast-growing type of brain cancer and the most common form of aggressive brain cancer in adults.\n<\/p><a class=\"oxy-container-link-130-247 oxy-container-link od-button od-home-control od-home-control--navy od-focus-area-action\" href=\"\/disease-info\/glioblastoma\/\" target=\"_self\" aria-label=\"Learn more about Glioblastoma\"><span class=\"oxy-text-130-245 oxy-text od-link-label\">\nLearn More\n<\/span><div class=\"oxy-svg-icon2-130-246 oxy-svg-icon2 od-link-icon od-focus-area-arrow\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"24\" height=\"24\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><path d=\"M5 12h14\"><\/path><path d=\"m12 5 7 7-7 7\"><\/path><\/svg>\n<\/div><\/a><\/div><\/article><\/div><\/div><\/section><section class=\"oxy-container-130-277 oxy-container od-section od-focus-science\" aria-labelledby=\"focus-science-title\"><div class=\"oxy-container-130-276 oxy-container od-container\"><div class=\"oxy-container-130-275 oxy-container od-focus-science-content\"><h2 class=\"oxy-text-130-253 oxy-text od-section-title od-focus-science-title\" id=\"focus-science-title\">\nOur Scientific Approach\n<\/h2><div class=\"oxy-container-130-274 oxy-container od-focus-science-grid\"><article class=\"oxy-container-130-258 oxy-container od-focus-science-card\"><header class=\"oxy-container-130-256 oxy-container od-focus-science-heading\"><span class=\"oxy-text-130-254 oxy-text od-focus-science-marker\" aria-hidden=\"true\">\n\n<\/span><h3 class=\"oxy-text-130-255 oxy-text od-focus-science-card-title\">\nPatient-Centred Research\n<\/h3><\/header><p class=\"oxy-text-130-257 oxy-text od-body-small\">\nWe design our research programmes with patients at the centre, focusing on outcomes that matter most to those living with rare diseases and their families.\n<\/p><\/article><article class=\"oxy-container-130-263 oxy-container od-focus-science-card\"><header class=\"oxy-container-130-261 oxy-container od-focus-science-heading\"><span class=\"oxy-text-130-259 oxy-text od-focus-science-marker od-focus-marker--purple\" aria-hidden=\"true\">\n\n<\/span><h3 class=\"oxy-text-130-260 oxy-text od-focus-science-card-title\">\nScientific Excellence\n<\/h3><\/header><p class=\"oxy-text-130-262 oxy-text od-body-small\">\nOur research is guided by rigorous scientific standards and conducted in collaboration with leading experts in each therapeutic area.\n<\/p><\/article><article class=\"oxy-container-130-268 oxy-container od-focus-science-card\"><header class=\"oxy-container-130-266 oxy-container od-focus-science-heading\"><span class=\"oxy-text-130-264 oxy-text od-focus-science-marker od-focus-marker--navy\" aria-hidden=\"true\">\n\n<\/span><h3 class=\"oxy-text-130-265 oxy-text od-focus-science-card-title\">\nRegulatory Expertise\n<\/h3><\/header><p class=\"oxy-text-130-267 oxy-text od-body-small\">\nWe work closely with regulatory authorities across multiple regions to ensure our therapies meet the highest standards for safety and efficacy.\n<\/p><\/article><article class=\"oxy-container-130-273 oxy-container od-focus-science-card\"><header class=\"oxy-container-130-271 oxy-container od-focus-science-heading\"><span class=\"oxy-text-130-269 oxy-text od-focus-science-marker\" aria-hidden=\"true\">\n\n<\/span><h3 class=\"oxy-text-130-270 oxy-text od-focus-science-card-title\">\nLong-Term Commitment\n<\/h3><\/header><p class=\"oxy-text-130-272 oxy-text od-body-small\">\nOur commitment extends beyond initial approval, with ongoing research to better understand long-term outcomes and optimise treatment strategies.\n<\/p><\/article><\/div><\/div><\/div><\/section><section class=\"oxy-container-130-286 oxy-container od-focus-banner\" aria-label=\"Research that supports patients\"><img decoding=\"async\" class=\"oxy-image-130-278 oxy-image od-focus-banner-image\" src=\"https:\/\/funny-fermi.104-248-174-66.plesk.page\/wp-content\/uploads\/2026\/09\/Painting_1050.jpg\" alt=\"Family enjoying quality time together, reflecting the lives our research aims to enrich\" loading=\"lazy\"><div class=\"oxy-container-130-279 oxy-container od-focus-banner-shade\" aria-hidden=\"true\"><\/div><div class=\"oxy-container-130-285 oxy-container od-container od-focus-banner-container\"><div class=\"oxy-container-130-284 oxy-container od-focus-banner-copy\"><p class=\"oxy-text-130-280 oxy-text od-focus-banner-text\">\nBehind every research programme is a patient whose life we strive to support.\n<\/p><a class=\"oxy-container-link-130-283 oxy-container-link od-partner-banner-link\" href=\"\/disease-info\/\" target=\"_self\"><span class=\"oxy-text-130-281 oxy-text od-link-label\">\nLearn about rare diseases\n<\/span><div class=\"oxy-svg-icon2-130-282 oxy-svg-icon2 od-partner-banner-arrow\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"14\" height=\"14\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><path d=\"M5 12h14\"><\/path><path d=\"m12 5 7 7-7 7\"><\/path><\/svg>\n<\/div><\/a><\/div><\/div><\/section><section class=\"oxy-container-130-307 oxy-container od-section od-section--muted od-focus-products\" aria-labelledby=\"focus-products-title\"><div class=\"oxy-container-130-306 oxy-container od-container od-focus-products-container\"><header class=\"oxy-container-130-290 oxy-container od-focus-products-heading\"><div class=\"oxy-container-130-287 oxy-container od-section-marker od-marker--center\" aria-hidden=\"true\"><\/div><h2 class=\"oxy-text-130-288 oxy-text od-section-title od-focus-products-title\" id=\"focus-products-title\">\nOur Products\n<\/h2><p class=\"oxy-text-130-289 oxy-text od-body od-focus-products-lead\">\nThis section lists Orphalan's approved therapies by therapeutic area.\n<\/p><\/header><div class=\"oxy-container-130-302 oxy-container od-focus-product-grid\"><a class=\"oxy-container-link-130-296 oxy-container-link od-focus-product-card\" href=\"\/products\/#cuprior\" target=\"_self\"><div class=\"oxy-container-130-292 oxy-container od-focus-product-icon\"><div class=\"oxy-svg-icon2-130-291 oxy-svg-icon2 od-focus-product-symbol\">\n<svg aria-hidden=\"true\" fill=\"none\" stroke=\"currentColor\" viewBox=\"0 0 24 24\"><path stroke-linecap=\"round\" stroke-linejoin=\"round\" stroke-width=\"1.5\" d=\"M9.75 3.104v5.714a2.25 2.25 0 01-.659 1.591L5 14.5M9.75 3.104c-.251.023-.501.05-.75.082m.75-.082a24.301 24.301 0 014.5 0m0 0v5.714c0 .597.237 1.17.659 1.591L19.8 15.3M14.25 3.104c.251.023.501.05.75.082M19.8 15.3l-1.57.393A9.065 9.065 0 0112 15a9.065 9.065 0 00-6.23-.693L5 14.5m14.8.8l1.402 1.402c1.232 1.232.65 3.318-1.067 3.611A48.309 48.309 0 0112 21a48.309 48.309 0 01-8.135-.687c-1.718-.293-2.3-2.379-1.067-3.61L5 14.5\"><\/path><\/svg>\n<\/div><\/div><h3 class=\"oxy-text-130-293 oxy-text od-focus-product-title\">\nCuprior<sup>\u00ae<\/sup> (EU)\n<\/h3><p class=\"oxy-text-130-294 oxy-text od-focus-product-disease\">\nWilson's Disease\n<\/p><p class=\"oxy-text-130-295 oxy-text od-focus-product-note\">\nAlso marketed as Cuvrior\u00ae in the US and Ku Pei Ou\u00ae in China\n<\/p><\/a><a class=\"oxy-container-link-130-301 oxy-container-link od-focus-product-card\" href=\"\/products\/#kigabeq\" target=\"_self\"><div class=\"oxy-container-130-298 oxy-container od-focus-product-icon\"><div class=\"oxy-svg-icon2-130-297 oxy-svg-icon2 od-focus-product-symbol\">\n<svg aria-hidden=\"true\" xmlns=\"http:\/\/www.w3.org\/2000\/svg\" width=\"24\" height=\"24\" viewBox=\"0 0 24 24\" fill=\"none\" stroke=\"currentColor\" stroke-width=\"2\" stroke-linecap=\"round\" stroke-linejoin=\"round\"><circle cx=\"12\" cy=\"12\" r=\"1\"><\/circle><path d=\"M20.2 20.2c2.04-2.03.02-7.36-4.5-11.9-4.54-4.52-9.87-6.54-11.9-4.5-2.04 2.03-.02 7.36 4.5 11.9 4.54 4.52 9.87 6.54 11.9 4.5Z\"><\/path><path d=\"M15.7 15.7c4.52-4.54 6.54-9.87 4.5-11.9-2.03-2.04-7.36-.02-11.9 4.5-4.52 4.54-6.54 9.87-4.5 11.9 2.03 2.04 7.36.02 11.9-4.5Z\"><\/path><\/svg>\n<\/div><\/div><h3 class=\"oxy-text-130-299 oxy-text od-focus-product-title\">\nKigabeq<sup>\u00ae<\/sup> (EU)\n<\/h3><p class=\"oxy-text-130-300 oxy-text od-focus-product-disease od-focus-product-disease--last\">\nWest's Syndrome\n<\/p><\/a><\/div><div class=\"oxy-container-130-305 oxy-container od-focus-product-actions\"><a class=\"oxy-text-link-130-303 oxy-text-link od-button od-home-control od-home-control--navy\" href=\"\/products\/\" target=\"_self\">\nView All Products\n<\/a><a class=\"oxy-text-link-130-304 oxy-text-link od-button od-home-control od-home-control--subtle\" href=\"\/pipeline\/\" target=\"_self\">\nDevelopment Pipeline\n<\/a><\/div><\/div><\/section><aside class=\"oxy-container-130-315 oxy-container od-approval-strip\" aria-label=\"Content approval information\"><div class=\"oxy-container-130-314 oxy-container od-container\"><div class=\"oxy-container-130-313 oxy-container od-approval-layout\"><div class=\"oxy-container-130-311 oxy-container od-approval-code\"><span class=\"oxy-text-130-308 oxy-text od-approval-text\">\nMLR Approval Code: ORP-EU-2026-001\n<\/span><span class=\"oxy-text-130-309 oxy-text od-approval-text\" aria-hidden=\"true\">\n\u2022\n<\/span><span class=\"oxy-text-130-310 oxy-text od-approval-text\">\nApproved: October 2026\n<\/span><\/div><p class=\"oxy-text-130-312 oxy-text od-approval-text\">\nFor Healthcare Professionals and Patients in Europe and regions where Orphalan operates\n<\/p><\/div><\/div><\/aside><\/div><\/div><\/main>","protected":false},"excerpt":{"rendered":"<p>Therapeutic Focus Areas Dedicated expertise in rare disease treatment Orphalan focuses on three therapeutic areas in rare diseases: metabolic disorders (including Wilson&#8217;s disease), West&#8217;s syndrome and glioblastoma. View Our Products Learn About Rare Diseases Back WE SOLVE Our Areas of Expertise We concentrate our efforts on rare diseases where specialised knowledge and dedicated research can [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_oxygen_hide_in_design_set":false,"_oxygen_tags":"","footnotes":""},"class_list":["post-130","page","type-page","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/pages\/130","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/comments?post=130"}],"version-history":[{"count":15,"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/pages\/130\/revisions"}],"predecessor-version":[{"id":1076,"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/pages\/130\/revisions\/1076"}],"wp:attachment":[{"href":"https:\/\/funny-fermi.104-248-174-66.plesk.page\/fr\/wp-json\/wp\/v2\/media?parent=130"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}